Translating genetic findings to targeted therapies for children with rare diseases – GT Pharma 2025

Name: Translating genetic findings to targeted therapies for children with rare diseases – GT Pharma 2025
Uploaded: 2026-05-27T09:35:07-07:00
Duration: 19 min 56 s
Description: GraphTalk Pharma & LifeScience 2025. Project AMIGO is the gateway to data-driven pediatric care. We unite industry and European top-tier (university) pediatric clinics to accelerate genetic diagnosis, targeted therapy, and clinical trials—all within a secure, federated data network. • Faster…

May 27, 2026
Length: 20 min

Nicola Götzenberger Presenter Subscribe

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GraphTalk Pharma & LifeScience 2025

Project AMIGO is the gateway to data-driven pediatric care. We unite industry and European top-tier (university) pediatric clinics to accelerate genetic diagnosis, targeted therapy, and clinical trials—all within a secure, federated data network.

Faster Patient Access: Compress the diagnostic timeline so children can benefit from effective treatments sooner.
Precise Targeting: Pinpoint relevant patient groups for new or existing solutions, enhancing success rates.
Real-Time Insights: Harness ongoing data on disease progression and therapeutic responses to guide strategic decisions.

AMIGO leverages mixed funding from government, academia, and industry to ensure a sustainable approach that can truly transform pediatric healthcare for the long term.

Speakers

Nicola Götzenberger - Global Liaison Manager, LMU Klinikum
Daniel Weiss - Computational Scientist, LMU Klinikum